Beyond Rare: CI Analysis of the Evolving Gaucher’s Disease...

a adăugat un sunet Health

2025-06-23 12:48:37 -

Beyond Rare: CI Analysis of the Evolving Gaucher’s Disease Treatment Landscape

Gaucher’s Disease, a rare lysosomal storage disorder, is entering a new era of targeted therapies and patient-centered treatment. No longer managed solely by biweekly enzyme replacement, the field is evolving with oral agents, precision diagnostics, and the promise of gene therapy. As clinical science advances, Gaucher’s Disease is emerging as a model for rare genetic disease...

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